@inproceedings{inproceedings9c8e3aad, title = {Stable and cost-effective production of GCASE-OPT using a low MOI lentiviral approach for enzyme replacement therapy in gaucher disease: development of L20_HEF1A_GBA-OPT-R534H, a stable human cell line}, author = {Suardi, Gabriela Aparecida Marcondes and Wiezel, Cláudia Emília Vieira and Tirapelli, Daniela Pretti da Cunha and Ramos, Ester Silveira and Almeida, Vania de and Siciliano, Velia and Gerson, Stanton and Weiss, Ron and Fontes, Aparecida Maria}, year = {2024}, publisher = {Sociedade Brasileira de Genética (SBG)}, booktitle = {International Congress of the Brazilian Genetics Society} }