233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15–17 September 2017 (2018)
- Authors:
- Lostal, William

- Urtizberea, J. Andoni
- Richard, Isabelle

- Alonso-Jiménez, Alicia

- Carlier, Robert-Yves
- Carson, Vincent

- Diaz-Manera, Jordi

- Eymard, Bruno
- Fardeau, Michel
- Gourlay, Marie-Laurence
- Guglieri, Michela

- Hogrel, Jean-Yves

- Kullmann, Bruno
- Levy, Jennifer

- Ono, Yasuko

- Prigent, Hélène

- Saenz, Amets

- Semplicini, Claudio

- Vainzof, Mariz

- Vissing, John

- Maggie, Walter

- Lostal, William
- Autor USP: VAINZOF, MARIZ - IB
- Unidade: IB
- DOI: 10.1016/j.nmd.2018.03.010
- Subjects: DISTROFIA MUSCULAR; MUTAÇÃO GENÉTICA; ENZIMAS; AMINOÁCIDOS; ENSAIO CLÍNICO
- Agências de fomento:
- Financiado pela European Neuromuscular (ENMC)
- Finaciado pela Association Française contre les Myopathies (France)
- Financiado pela Deutsche Gesellschaft für Muskelkranke (Germany)
- Financiado pela Muscular Dystrophy UK
- Financiado pela Muskelsvindfonden (Denmark)
- Financiado pela Prinses Beatrix Spierfonds (The Netherlands)
- Financiado pela Schweizerische Stiftung für die Erforschung der Muskelkrankheiten (Switzerland)
- Financiado pela Telethon Foundation (Italy)
- Financiado pela Spierziekten Nederland (The Netherlands)
- Financiado pela Associated members
- Financiado pela Neuromuscular Association (Finland)
- Language: Inglês
- Imprenta:
- Source:
- Título: Neuromuscular Disorders
- ISSN: 0960-3966
- Volume/Número/Paginação/Ano: v. 28, p. 540-549, 2018
- Status:
- Artigo possui acesso gratuito no site do editor (Bronze Open Access)
- Versão do Documento:
- Versão publicada (Published version)
- Acessar versão aberta:
-
ABNT
LOSTAL, William et al. 233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15–17 September 2017. Neuromuscular Disorders, v. 28, p. 540-549, 2018Tradução . . Disponível em: https://doi.org/10.1016/j.nmd.2018.03.010. Acesso em: 06 maio 2026. -
APA
Lostal, W., Urtizberea, J. A., Richard, I., Alonso-Jiménez, A., Carlier, R. -Y., Carson, V., et al. (2018). 233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15–17 September 2017. Neuromuscular Disorders, 28, 540-549. doi:10.1016/j.nmd.2018.03.010 -
NLM
Lostal W, Urtizberea JA, Richard I, Alonso-Jiménez A, Carlier R-Y, Carson V, Diaz-Manera J, Eymard B, Fardeau M, Gourlay M-L, Guglieri M, Hogrel J-Y, Kullmann B, Levy J, Ono Y, Prigent H, Saenz A, Semplicini C, Vainzof M, Vissing J, Maggie W. 233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15–17 September 2017 [Internet]. Neuromuscular Disorders. 2018 ; 28 540-549.[citado 2026 maio 06 ] Available from: https://doi.org/10.1016/j.nmd.2018.03.010 -
Vancouver
Lostal W, Urtizberea JA, Richard I, Alonso-Jiménez A, Carlier R-Y, Carson V, Diaz-Manera J, Eymard B, Fardeau M, Gourlay M-L, Guglieri M, Hogrel J-Y, Kullmann B, Levy J, Ono Y, Prigent H, Saenz A, Semplicini C, Vainzof M, Vissing J, Maggie W. 233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15–17 September 2017 [Internet]. Neuromuscular Disorders. 2018 ; 28 540-549.[citado 2026 maio 06 ] Available from: https://doi.org/10.1016/j.nmd.2018.03.010 - Therapeutic potential of murine mesenchymal stem cells (MSC) from adipose tissue in the treatment of muscular dystrophy in the new double mutant mouse model for the genes Dystrophin and Large
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